Michelle Corbet at The Daily Memphian:
Over the past three years, nine babies with SCID-X1, more commonly known as “bubble boy disease,” have been treated with an experimental therapy that is now being heralded as a cure.
St. Jude Children’s Research Hospital president and CEO James Downing said in his 32 years at St. Jude, the children’s hospital has accomplished many milestones, but Wednesday’s announcement was particularly exciting — a cure.
“These patients are toddlers now who are responding to vaccinations and producing cells as they explore the world and live normal lives,” said principal investigator of the trial, Dr. Ewelina Mamcarz, of the St. Jude Department of Bone Marrow Transplantation and Cellular Therapy.
The results are being published in the April 18 issue of the New England Journal of Medicine.
This is simply amazing.